"The Times They Are a-Changin'." In reply to El-Zaidy et al.: AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study with a Prospective Natural History Cohort

Laurent Servais
2019 Journal of Neuromuscular Diseases  
doi:10.3233/jnd-199001 pmid:31476168 fatcat:yx5nwclgtbabflqinbhy4kfccy