Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa

Jeroen Bremer, Olivier Bornert, Alexander Nyström, Antoni Gostynski, Marcel F Jonkman, Annemieke Aartsma-Rus, Peter C van den Akker, Anna MG Pasmooij
2016 Molecular Therapy: Nucleic Acids  
doi:10.1038/mtna.2016.87 pmid:27754488 fatcat:rvrho4bsrjewjjxldmnm3ainn4