Glycomimetic-based pharmacological chaperones for lysosomal storage disorders: lessons from Gaucher, GM1-gangliosidosis and Fabry diseases

Elena M. Sánchez-Fernández, José M. García Fernández, Carmen Ortiz Mellet
2016 Chemical Communications  
Recent advancements and future outlook on pharmacological chaperones for lysosomal storage disorders using glycomimetics are discussed.
doi:10.1039/c6cc01564f pmid:27043200 fatcat:2spitoavmffhpdw32vijcziayu