Successful Reconstitution of Immunity in ADA-SCID by Stem Cell Gene Therapy Following Cessation of PEG-ADA and Use of Mild Preconditioning

H. Bobby Gaspar, Emma Bjorkegren, Kate Parsley, Kimberly C. Gilmour, Doug King, Joanna Sinclair, Fang Zhang, Aris Giannakopoulos, Stuart Adams, Lynette D. Fairbanks, Jane Gaspar, Lesley Henderson (+5 others)
2006 Molecular Therapy  
doi:10.1016/j.ymthe.2006.06.007 pmid:16905365 fatcat:aunwccju5jdxxaen5bgoq3k4jm