Bremer, Bornert, Nyström, Gostynski, Jonkman, Aartsma-Rus, Akker, Pasmooij, 2016. Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa.. https://doi.org/10.1038/mtna.2016.87