@article{bremer_bornert_nyström_gostynski_jonkman_aartsma-rus_akker_pasmooij_2016, title={Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa}, DOI={10.1038/mtna.2016.87}, publisher={Elsevier BV}, author={Bremer and Bornert and Nyström and Gostynski and Jonkman and Aartsma-Rus and Akker and Pasmooij}, year={2016} }