Gene Therapy container_uzlrb5iejzelrkon3vg6jiu73u

Springer Science and Business Media LLC

Homepage URLs

http://www.naturesj.com/gt/

Example Publications

Lentiviral standards to determine the sensitivity of assays that quantify lentiviral vector copy numbers and genomic insertion sites in cells

Guillaume Corre, Ababacar Seye, Sophie Frin, Maxime Ferrand, Kathrin Winkler, Cyril Luc, Fabien Dorange, Céline J. Rocca, Anne Galy
2022 | Gene Therapy
doi:10.1038/s41434-022-00315-8   pmcid:PMC9482878  

AAV2-VEGF-B gene therapy failed to induce angiogenesis in ischemic porcine myocardium due to inflammatory responses

Henna Korpela, Jaakko Lampela, Jonna Airaksinen, Niko Järveläinen, Satu Siimes, Kaisa Valli, Tiina Nieminen, Minttu Turunen, Maria Grönman, Antti Saraste, Juhani Knuuti, Mikko Hakulinen (+4 others)
2022 | Gene Therapy
doi:10.1038/s41434-022-00322-9   pmcid:PMC9684066  

Lack of germline transmission in male mice following a single intravenous administration of AAV5-hFVIII-SQ gene therapy

Carlos Fonck, Cheng Su, Jeremy Arens, Elli Koziol, Jaydeep Srimani, Joshua Henshaw, Andrea Van Tuyl, Sundeep Chandra, Christian Vettermann, Charles A. O'Neill
2022 | Gene Therapy
doi:10.1038/s41434-022-00318-5   pmcid:PMC10457182  

Antisense oligonucleotides as a potential treatment for brain deficits observed in myotonic dystrophy type 1

Siham Ait Benichou, Dominic Jauvin, Thiéry De Serres-Bérard, Marion Pierre, Karen K. Ling, C. Frank Bennett, Frank Rigo, Genevieve Gourdon, Mohamed Chahine, Jack Puymirat
2022 | Gene Therapy
doi:10.1038/s41434-022-00316-7   pmcid:PMC9750879  
4,848
Known Releases
Preservation Summary [more]
3,501 preserved and accessble (bright)
1,197 preserved, inaccessible (dark)
150 no known preservation
Release Types
article-journal 4,806
editorial 29
unknown-type 12
letter 1
ISSN-L?  0969-7128
    Print:  0969-7128
    Electronic:  1476-5462
Wikidata  Q15763095
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